TY  - BOOK
AU  - Colavito,Mary C.
TI  - Gene therapy / 
T2  - Benjamin/Cummings special topics in biology series
SN  - 0805338195
U1  - 616.042 23
PY  - 2007///],
CY  - San Francisco : 
PB  - Pearson, 
KW  - Gene therapy
KW  - Genetic Therapy
N1  - pharmacy bookfair2016; Includes bibliographical references; Realizing the promise of gene therapy : successes, setbacks, and challenges -- Gene therapy methods. Identifying a disease that is likely to respond to gene therapy ; Isolating a functional copy of the gene ; Incorporating the gene into a carrier for gene delivery ; Determining whether the gene product is made --
Partial successes and ongoing trials. Gene therapy for severe combined immune deficiency (ADA-SCID) ; Gene therapy for cystic fibrosis ; Gene therapy for canavan disease --
Setbacks. Immune reactions targeting cells carrying the vector ; Inadvertent activation of cancer causing genes by a vector ; Insufficient numbers of cells producing the gene product
ER  -